Despite significant advancements in spinal muscular atrophy (SMA) management, unmet needs persist, especially for patients ...

FDA-approved treatments for spinal muscular atrophy differ in their mechanisms of action, safety profiles, and administration ...

Reason for decision Anticipate the topic will be of importance to patients, carers, professionals, commissioners and the health of the public to ensure clinical benefit is realised, inequalities in ...

Affordable generic version of SMA drug Risdiplam soon available in India, offering hope to patients and activists.

Those with spinal muscular atrophy can get emotional support by building an SMA support system that includes SMA communities ...

Manchester United captain Bruno Fernandes has issued a message after he was joined by a disabled mascot at Old Trafford ahead ...

Funding medical research is about more than just numbers. It's real people,” says Ryan Manriquez, president of the UC ...

PTC Therapeutics, Inc.’s PTCT share price has surged by 6.72%, which has investors questioning if this is right time to sell.

It's that time of year when you can become a Hero for Hope and donate to ABC15's annual Telethon for Phoenix Children's ...

Imagine the joy of holding your newborn for the first time, only to hear doctors say your baby would live to the age of two.