It was submitted that why can't the Indian government negotiate with Roche to make the medicine for the rare disorder ...

The Supreme Court on Friday asked the Centre and the manufacturer of the drug Risdiplam, which is used for the treatment of ...

The NIH is considering a catastrophic cut to indirect cost reimbursements for public universities, which would hurt the ...

Can the medicine for treatment of rare disorder spinal muscular atrophy (SMA) be made available at lower price in India if it ...

FDA-approved treatments for spinal muscular atrophy differ in their mechanisms of action, safety profiles, and administration ...

Children with SMA in the U.K. can switch treatments based on practical needs and preferences without unexpected disease ...

Amino acid balance could play a role in SMA, as a study showed acids able to influence nervous system function were ...

Intrathecal treatment with a vector-based gene therapy was associated with a greater improvement in motor function at 52 weeks compared with sham in patients aged 2 to 18 years with spinal muscular ...

The FDA has accepted for Priority Review the BLA for apitegromab for the improvement of motor function in patients with spinal muscular atrophy.

In less than two weeks, the country came together and collected over KGS 510 million (USD 5.9 million), displaying ...

Gene therapy treatment gives Baby Kiama a lifeline, saving him from world’s most expensive drug that he needed to slow down a ...