University of California18h
Facing cuts to biomedical research, a UC student leader shares his story
Funding medical research is about more than just numbers. It's real people,” says Ryan Manriquez, president of the UC ...
The American Journal of Managed Care3d
Key Considerations for Choosing the Right SMA Treatment
FDA-approved treatments for spinal muscular atrophy differ in their mechanisms of action, safety profiles, and administration ...
'Something special' - Bruno Fernandes issues glowing message after disabled mascot with spinal muscular atrophy joins Man Utd captain in leading out Red Devils for M…
Manchester United captain Bruno Fernandes has issued a message after he was joined by a disabled mascot at Old Trafford ahead ...
Natco Pharma shares legal update on Risdiplam patent; stock up 3%
Natco Pharma on Tuesday shared a legal update on the legal proceedings on the Risdiplam compound (used for treating spinal ...
ABC15 Arizona21h
Scottsdale boy beats the odds, paves the way for others at Phoenix Children's and beyond
It's that time of year when you can become a Hero for Hope and donate to ABC15's annual Telethon for Phoenix Children's ...
Managed Healthcare Executive13d
FDA Grants Priority Review BLA for Spinal Muscular Atrophy Drug, Apitegromab
A Prescription Drug User Fee Act (PDUFA) target action date for apitegromab has been set for Sept. 22, 2025.
The Week13d
How Delhi High Court's latest verdict is a boon for spinal muscular atrophy patients
A rare genetic condition, Spinal Muscular Atrophy (SMA) affects one in 7,000 people in India. It mostly affects children and ...
The Indian Express12d
Indian company can now make Spinal Muscular Atrophy drug, High Court cites public interest
In what could be promising news for patients battling spinal muscular atrophy (SMA), the Delhi High Court has refused to ...
Rheumatology Advisor6d
Apitegromab Gets Priority Review for Spinal Muscular Atrophy
The FDA has accepted for Priority Review the BLA for apitegromab for the improvement of motor function in patients with spinal muscular atrophy.
Scholar Rock Application for Spinal Muscular Atrophy Treatment Gets FDA Approval
Apitegromab is an investigational treatment aimed at improving motor function for people living with spinal muscular atrophy. Scholar Rock said it has also submitted and received validation for its ...