Somewhere in an operating room this spring, a neurosurgeon did something that has never been done before: while removing a ...

Gene therapy has experienced an increasing number of successful human clinical trials, leading to numerous FDA-approved therapies based on recombinant viruses for rare disease, cancer, and other ...

Summary: Researchers demonstrated that an experimental, systemic gene therapy can shield the central nervous system from the devastating cognitive decline and structural damage caused by ...

Gene therapy represents one of medicine’s most ambitious attempts to treat disease at its root cause by altering the genetic code itself. The approach works by recovering the functions of critical ...

Viral vectors dominate gene therapy, with lentivirus, adenovirus, and AAV being key players, each with unique advantages and limitations. Non-viral vectors, such as lipid nanoparticles and GalNAc, ...

A key claim by the company MedTherapy is a major reduction in production timelines. While gene therapies typically take weeks ...

The firm will evaluate its adeno-associated virus-based gene therapy, TGX-007, in patients with newly diagnosed or recurrent tumors.

For generations, Sickle Cell Disease has been a devastating illness affecting millions of people around the world, ...

Gene therapy achieved its first major breakthroughs in the early 1990s with the treatment of a rare disease called severe combined immunodeficiency. However, the field was dealt a serious setback in ...